Ultragenyx stock gains on FDA priority review acceptance By Investing.com

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Ultragenyx Pharmaceutical Inc. shares rose after the FDA accepted its Biologics License Application for DTX401, a gene therapy for Glycogen Storage Disease Type Ia, granting it Priority Review. The FDA set an action date of August 23, 2026, for the potential approval of DTX401, which would be the first treatment to address the underlying cause of GSDIa. Clinical data showed patients treated with DTX401 experienced reductions in cornstarch intake, improved euglycemia, and enhanced quality of life.

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